Global Gene Therapy for Mucopolysaccharidosis Market Size, Status and Forecast 2021-2027

  • Published Date : 05-05-2021
  • Pages : 91
  • Report Id : 26880
  • Categories : Healthcare

Mucopolysaccharidosis consists of a group of more than 40 genetic disorders that forms a part of lysosomal storage disease. They are caused by an inherited deficiency of an enzyme involved in the degradation of acid glycosaminoglycans (GAGs), which was previously known as mucopolysaccharidosis. All of the mucopolysaccharidoses are rare, autosomal recessive, except for mucopolysaccharidosis III, as it is X-linked.
Over the past few years, gene therapy has emerged as one of the most exciting approaches for the treatment of mucopolysaccharidosis. One of the promising therapy is replacement gene therapy, which replaces faulty genes with normal ones in the body. It is considered to be a potential cure to mucopolysaccharidoses and a promising option in the long run.
In 2020, the global Gene Therapy for Mucopolysaccharidosis market size was xx million US$ and it is expected to reach xx million US$ by the end of 2027, with a CAGR of xx% during 2021-2027.

This report focuses on the global Gene Therapy for Mucopolysaccharidosis status, future forecast, growth opportunity, key market and key players. The study objectives are to present the Gene Therapy for Mucopolysaccharidosis development in United States, Europe and China.

The key players covered in this study
Sangamo Therapeutics
Swedish Orphan Biovitrum
uniQure
...

Market segment by Type, the product can be split into
Intravenous
ICV
Intracerebral
Intracisternal

Market segment by Application, split into
Mucopolysaccharidosis I
Mucopolysaccharidosis II
Mucopolysaccharidosis III A
Mucopolysaccharidosis III B

Market segment by Regions/Countries, this report covers
United States
Europe
China
Japan
Southeast Asia
India
Central & South America

The study objectives of this report are:
To analyze global Gene Therapy for Mucopolysaccharidosis status, future forecast, growth opportunity, key market and key players.
To present the Gene Therapy for Mucopolysaccharidosis development in United States, Europe and China.
To strategically profile the key players and comprehensively analyze their development plan and strategies.
To define, describe and forecast the market by product type, market and key regions.

In this study, the years considered to estimate the market size of Gene Therapy for Mucopolysaccharidosis are as follows:
History Year: 2016-2020
Base Year: 2020
Estimated Year: 2021
Forecast Year 2021 to 2027
For the data information by region, company, type and application, 2020 is considered as the base year. Whenever data information was unavailable for the base year, the prior year has been considered.


Table of Contents

1 Report Overview
1.1 Study Scope
1.2 Key Market Segments
1.3 Players Covered
1.4 Market Analysis by Type
1.4.1 Global Gene Therapy for Mucopolysaccharidosis Market Size Growth Rate by Type ( 2016-2027)
1.4.2 Intravenous
1.4.3 ICV
1.4.4 Intracerebral
1.4.5 Intracisternal
1.5 Market by Application
1.5.1 Global Gene Therapy for Mucopolysaccharidosis Market Share by Application ( 2016-2027)
1.5.2 Mucopolysaccharidosis I
1.5.3 Mucopolysaccharidosis II
1.5.4 Mucopolysaccharidosis III A
1.5.5 Mucopolysaccharidosis III B
1.6 Study Objectives
1.7 Years Considered

2 Global Growth Trends
2.1 Gene Therapy for Mucopolysaccharidosis Market Size
2.2 Gene Therapy for Mucopolysaccharidosis Growth Trends by Regions
2.2.1 Gene Therapy for Mucopolysaccharidosis Market Size by Regions ( 2016-2027)
2.2.2 Gene Therapy for Mucopolysaccharidosis Market Share by Regions ( 2016-2021)
2.3 Industry Trends
2.3.1 Market Top Trends
2.3.2 Market Drivers
2.3.3 Market Opportunities

3 Market Share by Key Players
3.1 Gene Therapy for Mucopolysaccharidosis Market Size by Manufacturers
3.1.1 Global Gene Therapy for Mucopolysaccharidosis Revenue by Manufacturers ( 2016-2021)
3.1.2 Global Gene Therapy for Mucopolysaccharidosis Revenue Market Share by Manufacturers ( 2016-2021)
3.1.3 Global Gene Therapy for Mucopolysaccharidosis Market Concentration Ratio (CR5 and HHI)
3.2 Gene Therapy for Mucopolysaccharidosis Key Players Head office and Area Served
3.3 Key Players Gene Therapy for Mucopolysaccharidosis Product/Solution/Service
3.4 Date of Enter into Gene Therapy for Mucopolysaccharidosis Market
3.5 Mergers & Acquisitions, Expansion Plans

4 Breakdown Data by Type and Application
4.1 Global Gene Therapy for Mucopolysaccharidosis Market Size by Type ( 2016-2021)
4.2 Global Gene Therapy for Mucopolysaccharidosis Market Size by Application ( 2016-2021)

5 United States
5.1 United States Gene Therapy for Mucopolysaccharidosis Market Size ( 2016-2021)
5.2 Gene Therapy for Mucopolysaccharidosis Key Players in United States
5.3 United States Gene Therapy for Mucopolysaccharidosis Market Size by Type
5.4 United States Gene Therapy for Mucopolysaccharidosis Market Size by Application

6 Europe
6.1 Europe Gene Therapy for Mucopolysaccharidosis Market Size ( 2016-2021)
6.2 Gene Therapy for Mucopolysaccharidosis Key Players in Europe
6.3 Europe Gene Therapy for Mucopolysaccharidosis Market Size by Type
6.4 Europe Gene Therapy for Mucopolysaccharidosis Market Size by Application

7 China
7.1 China Gene Therapy for Mucopolysaccharidosis Market Size ( 2016-2021)
7.2 Gene Therapy for Mucopolysaccharidosis Key Players in China
7.3 China Gene Therapy for Mucopolysaccharidosis Market Size by Type
7.4 China Gene Therapy for Mucopolysaccharidosis Market Size by Application

8 Japan
8.1 Japan Gene Therapy for Mucopolysaccharidosis Market Size ( 2016-2021)
8.2 Gene Therapy for Mucopolysaccharidosis Key Players in Japan
8.3 Japan Gene Therapy for Mucopolysaccharidosis Market Size by Type
8.4 Japan Gene Therapy for Mucopolysaccharidosis Market Size by Application

9 Southeast Asia
9.1 Southeast Asia Gene Therapy for Mucopolysaccharidosis Market Size ( 2016-2021)
9.2 Gene Therapy for Mucopolysaccharidosis Key Players in Southeast Asia
9.3 Southeast Asia Gene Therapy for Mucopolysaccharidosis Market Size by Type
9.4 Southeast Asia Gene Therapy for Mucopolysaccharidosis Market Size by Application

10 India
10.1 India Gene Therapy for Mucopolysaccharidosis Market Size ( 2016-2021)
10.2 Gene Therapy for Mucopolysaccharidosis Key Players in India
10.3 India Gene Therapy for Mucopolysaccharidosis Market Size by Type
10.4 India Gene Therapy for Mucopolysaccharidosis Market Size by Application

11 Central & South America
11.1 Central & South America Gene Therapy for Mucopolysaccharidosis Market Size ( 2016-2021)
11.2 Gene Therapy for Mucopolysaccharidosis Key Players in Central & South America
11.3 Central & South America Gene Therapy for Mucopolysaccharidosis Market Size by Type
11.4 Central & South America Gene Therapy for Mucopolysaccharidosis Market Size by Application

12 International Players Profiles
12.1 Sangamo Therapeutics
12.1.1 Sangamo Therapeutics Company Details
12.1.2 Company Description and Business Overview
12.1.3 Gene Therapy for Mucopolysaccharidosis Introduction
12.1.4 Sangamo Therapeutics Revenue in Gene Therapy for Mucopolysaccharidosis Business ( 2016-2021)
12.1.5 Sangamo Therapeutics Recent Development
12.2 Swedish Orphan Biovitrum
12.2.1 Swedish Orphan Biovitrum Company Details
12.2.2 Company Description and Business Overview
12.2.3 Gene Therapy for Mucopolysaccharidosis Introduction
12.2.4 Swedish Orphan Biovitrum Revenue in Gene Therapy for Mucopolysaccharidosis Business ( 2016-2021)
12.2.5 Swedish Orphan Biovitrum Recent Development
12.3 uniQure
12.3.1 uniQure Company Details
12.3.2 Company Description and Business Overview
12.3.3 Gene Therapy for Mucopolysaccharidosis Introduction
12.3.4 uniQure Revenue in Gene Therapy for Mucopolysaccharidosis Business ( 2016-2021)
12.3.5 uniQure Recent Development

13 Market Forecast 2021-2027
13.1 Market Size Forecast by Regions
13.2 United States
13.3 Europe
13.4 China
13.5 Japan
13.6 Southeast Asia
13.7 India
13.8 Central & South America
13.9 Market Size Forecast by Product ( 2021-2027)
13.10 Market Size Forecast by Application ( 2021-2027)

14 Analyst's Viewpoints/Conclusions

15 Appendix
15.1 Research Methodology
15.1.1 Methodology/Research Approach
15.1.1.1 Research Programs/Design
15.1.1.2 Market Size Estimation
12.1.1.3 Market Breakdown and Data Triangulation
15.1.2 Data Source
15.1.2.1 Secondary Sources
15.1.2.2 Primary Sources
15.2 Disclaimer
15.3 Author Details

List of Tables and Figures

Table Gene Therapy for Mucopolysaccharidosis Key Market Segments
Table Key Players Gene Therapy for Mucopolysaccharidosis Covered
Table Global Gene Therapy for Mucopolysaccharidosis Market Size Growth Rate by Type 2016-2027 (Million US$)
Figure Global Gene Therapy for Mucopolysaccharidosis Market Size Market Share by Type 2016-2027
Figure Intravenous Figures
Table Key Players of Intravenous
Figure ICV Figures
Table Key Players of ICV
Figure Intracerebral Figures
Table Key Players of Intracerebral
Figure Intracisternal Figures
Table Key Players of Intracisternal
Table Global Gene Therapy for Mucopolysaccharidosis Market Size Growth by Application 2016-2027 (Million US$)
Figure Mucopolysaccharidosis I Case Studies
Figure Mucopolysaccharidosis II Case Studies
Figure Mucopolysaccharidosis III A Case Studies
Figure Mucopolysaccharidosis III B Case Studies
Figure Gene Therapy for Mucopolysaccharidosis Report Years Considered
Table Global Gene Therapy for Mucopolysaccharidosis Market Size 2016-2027 (Million US$)
Figure Global Gene Therapy for Mucopolysaccharidosis Market Size and Growth Rate 2016-2027 (Million US$)
Table Global Gene Therapy for Mucopolysaccharidosis Market Size by Regions 2016-2027 (Million US$)
Table Global Gene Therapy for Mucopolysaccharidosis Market Size by Regions 2016-2021 (Million US$)
Table Global Gene Therapy for Mucopolysaccharidosis Market Share by Regions 2016-2021
Figure Global Gene Therapy for Mucopolysaccharidosis Market Share by Regions 2016-2021
Figure Global Gene Therapy for Mucopolysaccharidosis Market Share by Regions 2021
Table Market Top Trends
Table Global Gene Therapy for Mucopolysaccharidosis Revenue by Manufacturers ( 2016-2021) (Million US$)
Table Global Gene Therapy for Mucopolysaccharidosis Market Share by Manufacturers ( 2016-2021)
Figure Global Gene Therapy for Mucopolysaccharidosis Market Share by Manufacturers in 2020
Table Global Gene Therapy for Mucopolysaccharidosis Manufacturers Market Concentration Ratio (CR5 and HHI)
Table Key Players Head office and Area Served
Table Key Players Gene Therapy for Mucopolysaccharidosis Product/Solution/Service
Table Date of Enter into Gene Therapy for Mucopolysaccharidosis Market
Table Mergers & Acquisitions, Expansion Plans
Table Global Gene Therapy for Mucopolysaccharidosis Market Size by Type ( 2016-2021) (Million US$)
Table Global Gene Therapy for Mucopolysaccharidosis Market Size Share by Type ( 2016-2021)
Figure Global Gene Therapy for Mucopolysaccharidosis Market Size Market Share by Type ( 2016-2021)
Table Global Gene Therapy for Mucopolysaccharidosis Market Size by Application ( 2016-2021) (Million US$)
Table Global Gene Therapy for Mucopolysaccharidosis Market Size Share by Application ( 2016-2021)
Figure Global Gene Therapy for Mucopolysaccharidosis Market Size Market Share by Application ( 2016-2021)
Figure Global Gene Therapy for Mucopolysaccharidosis Revenue Market Share by Application in 2020
Figure United States Gene Therapy for Mucopolysaccharidosis Market Size 2016-2021 (Million US$)
Table United States Key Players Gene Therapy for Mucopolysaccharidosis Revenue ( 2020-2021) (Million US$)
Table United States Key Players Gene Therapy for Mucopolysaccharidosis Market Share ( 2020-2021)
Table United States Gene Therapy for Mucopolysaccharidosis Market Size by Type ( 2016-2021) (Million US$)
Table United States Gene Therapy for Mucopolysaccharidosis Market Share by Type ( 2016-2021)
Table United States Gene Therapy for Mucopolysaccharidosis Market Size by Application ( 2016-2021) (Million US$)
Table United States Gene Therapy for Mucopolysaccharidosis Market Share by Application ( 2016-2021)
Figure Europe Gene Therapy for Mucopolysaccharidosis Market Size 2016-2021 (Million US$)
Table Europe Key Players Gene Therapy for Mucopolysaccharidosis Revenue ( 2020-2021) (Million US$)
Table Europe Key Players Gene Therapy for Mucopolysaccharidosis Market Share ( 2020-2021)
Table Europe Gene Therapy for Mucopolysaccharidosis Market Size by Type ( 2016-2021) (Million US$)
Table Europe Gene Therapy for Mucopolysaccharidosis Market Share by Type ( 2016-2021)
Table Europe Gene Therapy for Mucopolysaccharidosis Market Size by Application ( 2016-2021) (Million US$)
Table Europe Gene Therapy for Mucopolysaccharidosis Market Share by Application ( 2016-2021)
Figure China Gene Therapy for Mucopolysaccharidosis Market Size 2016-2021 (Million US$)
Table China Key Players Gene Therapy for Mucopolysaccharidosis Revenue ( 2020-2021) (Million US$)
Table China Key Players Gene Therapy for Mucopolysaccharidosis Market Share ( 2020-2021)
Table China Gene Therapy for Mucopolysaccharidosis Market Size by Type (2014- 20209) (Million US$)
Table China Gene Therapy for Mucopolysaccharidosis Market Share by Type ( 2016-2021)
Table China Gene Therapy for Mucopolysaccharidosis Market Size by Application ( 2016-2021) (Million US$)
Table China Gene Therapy for Mucopolysaccharidosis Market Share by Application ( 2016-2021)
Figure Japan Gene Therapy for Mucopolysaccharidosis Market Size 2016-2021 (Million US$)
Table Japan Key Players Gene Therapy for Mucopolysaccharidosis Revenue ( 2020-2021) (Million US$)
Table Japan Key Players Gene Therapy for Mucopolysaccharidosis Market Share ( 2020-2021)
Table Japan Gene Therapy for Mucopolysaccharidosis Market Size by Type ( 2016-2021) (Million US$)
Table Japan Gene Therapy for Mucopolysaccharidosis Market Share by Type ( 2016-2021)
Table Japan Gene Therapy for Mucopolysaccharidosis Market Size by Application ( 2016-2021) (Million US$)
Table Japan Gene Therapy for Mucopolysaccharidosis Market Share by Application ( 2016-2021)
Figure Southeast Asia Gene Therapy for Mucopolysaccharidosis Market Size 2016-2021 (Million US$)
Table Southeast Asia Key Players Gene Therapy for Mucopolysaccharidosis Revenue ( 2020-2021) (Million US$)
Table Southeast Asia Key Players Gene Therapy for Mucopolysaccharidosis Market Share ( 2020-2021)
Table Southeast Asia Gene Therapy for Mucopolysaccharidosis Market Size by Type ( 2016-2021) (Million US$)
Table Southeast Asia Gene Therapy for Mucopolysaccharidosis Market Share by Type ( 2016-2021)
Table Southeast Asia Gene Therapy for Mucopolysaccharidosis Market Size by Application ( 2016-2021) (Million US$)
Table Southeast Asia Gene Therapy for Mucopolysaccharidosis Market Share by Application ( 2016-2021)
Figure India Gene Therapy for Mucopolysaccharidosis Market Size 2016-2021 (Million US$)
Table India Key Players Gene Therapy for Mucopolysaccharidosis Revenue ( 2020-2021) (Million US$)
Table India Key Players Gene Therapy for Mucopolysaccharidosis Market Share ( 2020-2021)
Table India Gene Therapy for Mucopolysaccharidosis Market Size by Type ( 2016-2021) (Million US$)
Table India Gene Therapy for Mucopolysaccharidosis Market Share by Type ( 2016-2021)
Table India Gene Therapy for Mucopolysaccharidosis Market Size by Application ( 2016-2021) (Million US$)
Table India Gene Therapy for Mucopolysaccharidosis Market Share by Application ( 2016-2021)
Figure Central & South America Gene Therapy for Mucopolysaccharidosis Market Size 2016-2021 (Million US$)
Table Central & South America Key Players Gene Therapy for Mucopolysaccharidosis Revenue ( 2020-2021) (Million US$)
Table Central & South America Key Players Gene Therapy for Mucopolysaccharidosis Market Share ( 2020-2021)
Table Central & South America Gene Therapy for Mucopolysaccharidosis Market Size by Type ( 2016-2021) (Million US$)
Table Central & South America Gene Therapy for Mucopolysaccharidosis Market Share by Type ( 2016-2021)
Table Central & South America Gene Therapy for Mucopolysaccharidosis Market Size by Application ( 2016-2021) (Million US$)
Table Central & South America Gene Therapy for Mucopolysaccharidosis Market Share by Application ( 2016-2021)
Table Sangamo Therapeutics Company Details
Table Sangamo Therapeutics Revenue in Gene Therapy for Mucopolysaccharidosis Business ( 2016-2021) (Million US$)
Figure Sangamo Therapeutics Revenue Growth Rate in Gene Therapy for Mucopolysaccharidosis Business ( 2016-2021)
Table Sangamo Therapeutics Recent Development
Table Swedish Orphan Biovitrum Company Details
Table Swedish Orphan Biovitrum Revenue in Gene Therapy for Mucopolysaccharidosis Business ( 2016-2021)(Million US$)
Figure Swedish Orphan Biovitrum Revenue Growth Rate in Gene Therapy for Mucopolysaccharidosis Business ( 2016-2021)
Table Swedish Orphan Biovitrum Recent Development
Table uniQure Company Details
Table uniQure Revenue in Gene Therapy for Mucopolysaccharidosis Business ( 2016-2021)(Million US$)
Figure uniQure Revenue Growth Rate in Gene Therapy for Mucopolysaccharidosis Business ( 2016-2021)
Table uniQure Recent Development
Table Global Gene Therapy for Mucopolysaccharidosis Market Size by Regions (Million US$) 2021-2027
Figure Global Gene Therapy for Mucopolysaccharidosis Market Size Share by Regions ( 2021-2027)
Figure Global Gene Therapy for Mucopolysaccharidosis Market Size Share by Regions in 2027
Figure United States Gene Therapy for Mucopolysaccharidosis Market Size Forecast ( 2021-2027)(Million USD)
Figure Europe Gene Therapy for Mucopolysaccharidosis Market Size Forecast ( 2021-2027)(Million USD)
Figure China Gene Therapy for Mucopolysaccharidosis Market Size Forecast ( 2021-2027)(Million USD)
Figure Japan Gene Therapy for Mucopolysaccharidosis Market Size Forecast ( 2021-2027)(Million USD)
Figure Southeast Asia Gene Therapy for Mucopolysaccharidosis Market Size Forecast ( 2021-2027)(Million USD)
Figure India Gene Therapy for Mucopolysaccharidosis Market Size Forecast ( 2021-2027)(Million USD)
Figure Central & South America Gene Therapy for Mucopolysaccharidosis Market Size Forecast ( 2021-2027)(Million USD)
Table Global Gene Therapy for Mucopolysaccharidosis Market Size by Product ( 2021-2027) (Million US$)
Figure Global Gene Therapy for Mucopolysaccharidosis Market Size by Product ( 2021-2027)
Figure Global Gene Therapy for Mucopolysaccharidosis Market Size by Product in 2027
Table Global Gene Therapy for Mucopolysaccharidosis Market Size by Application ( 2021-2027) (Million US$)
Figure Global Gene Therapy for Mucopolysaccharidosis Market Size by Application ( 2021-2027)
Figure Global Gene Therapy for Mucopolysaccharidosis Market Size by Application in 2027
Table Research Programs/Design for This Report
Figure Bottom-up and Top-down Approaches for This Report
Figure Data Triangulation
Table Key Data Information from Secondary Sources
Table Key Data Information from Primary Sources

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